Comparison of enzymatic activity with evidence of engraftment in patients with inborn errors of metabolism receiving allogeneic marrow transplantation

Birth Defects Orig Artic Ser. 1986;22(1):135-52.
No abstract available

Publication types

  • Case Reports
  • Comparative Study
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Adenosine Deaminase / deficiency
  • Adolescent
  • Bone Marrow Transplantation*
  • Cerebroside-Sulfatase / blood
  • Child, Preschool
  • Chondro-4-Sulfatase / blood
  • Female
  • Graft Survival
  • Humans
  • Iduronidase / blood
  • Leukodystrophy, Metachromatic / therapy
  • Male
  • Metabolism, Inborn Errors / therapy*
  • Mucopolysaccharidoses / therapy
  • Mucopolysaccharidosis VI / therapy

Substances

  • Cerebroside-Sulfatase
  • Chondro-4-Sulfatase
  • Iduronidase
  • Adenosine Deaminase