Facilitating orphan drug development: Proceedings of the TREAT-NMD International Conference, December 2015, Washington, DC, USA
Neuromuscul Disord
.
2017 Jul;27(7):693-701.
doi: 10.1016/j.nmd.2017.02.013.
Epub 2017 Mar 4.
Authors
E P Hoffman
1
;
Workshop Participants
2
;
TREAT-NMD Alliance
2
Collaborators
Carsten Bonnemann
3
,
Marc Boutin
4
,
Bernard Brais
5
,
Filippo Buccella
6
,
Arthur Burghes
7
,
Christopher Coffey
8
,
Nabarun Dasgupta
9
,
Hugh Dawkins
10
,
Annamaria De Luca
11
,
Christopher Dowd
3
,
Tina Duong
12
,
Michelle Eagle
13
,
Richard Finkel
14
,
Pat Furlong
15
,
Cynthia Gagnon
5
,
Nathalie Goemans
16
,
Michela Guglieri
13
,
Yetrib Hathout
4
,
Nicholas Johnson
17
,
Emil Kakkis
18
,
Petra Kaufmann
3
,
Jonathan Kimmelman
5
,
Lawrence Korngut
19
,
Joyce Kullman
20
,
Hanns Lochmüller
13
,
Stefano Marini
6
,
Craig McDonald
21
,
Charles Mohan
22
,
Lauren Morgenroth
4
,
Hiroki Morizono
4
,
Kanneboyina Nagaraju
4
,
John Porter
3
,
Lori Reilly
4
,
Markus Rüegg
23
,
Joel Schneider
9
,
Pietro Spitali
24
,
Volker Straub
13
,
Lee Sweeney
25
,
Giorgio Tasca
26
,
Cathy Turner
13
,
Olav Veldhuizen
13
,
Jan Verschuuren
24
,
Susan Ward
27
,
Raffaella Willmann
23
Affiliations
1
Binghamton University - SUNY, USA. Electronic address: ehoffman@binghamton.edu.
2
Binghamton University - SUNY, USA.
3
Bethesda, MD, USA.
4
Washington, DC, USA.
5
Montreal, Quebec, Canada.
6
Rome, Italy.
7
Columbus, OH, USA.
8
Iowa City, IA, USA.
9
Boston, MA, USA.
10
Perth, Australia.
11
Bari, Italy.
12
Stanford, CA, USA.
13
Newcastle, UK.
14
Orlando, FL, USA.
15
Hackensack, NJ, USA.
16
Leuven, Belgium.
17
Salt Lake City, UT, USA.
18
Novato, CA, USA.
19
Calgary, Alberta, Canada.
20
Kansas City, MO, USA.
21
Davis, CA, USA.
22
Pittsburgh, PA, USA.
23
Basel, Switzerland.
24
Leiden, The Netherlands.
25
Gainesville, FL, USA.
26
Ottawa, Ontario, Canada.
27
Cambridge, MA, USA.
PMID:
28434909
DOI:
10.1016/j.nmd.2017.02.013
No abstract available
Publication types
Research Support, Non-U.S. Gov't
MeSH terms
Congresses as Topic
District of Columbia
Humans
Neuromuscular Diseases / drug therapy*
Orphan Drug Production*