Patients with Gaucher type 1: Switching from imiglucerase to miglustat therapy

Blood Cells Mol Dis. 2018 Feb:68:180-184. doi: 10.1016/j.bcmd.2017.01.007. Epub 2017 Jan 16.
No abstract available

Keywords: Gaucher; Imiglucerase; Substrate reduction therapy.

MeSH terms

  • 1-Deoxynojirimycin / analogs & derivatives*
  • 1-Deoxynojirimycin / therapeutic use
  • Adult
  • Enzyme Inhibitors / therapeutic use*
  • Enzyme Replacement Therapy
  • Female
  • Gaucher Disease / drug therapy*
  • Glucosylceramidase / therapeutic use*
  • Humans
  • Recombinant Proteins / therapeutic use
  • Treatment Outcome

Substances

  • Enzyme Inhibitors
  • Recombinant Proteins
  • 1-Deoxynojirimycin
  • miglustat
  • Glucosylceramidase
  • imiglucerase