Clinical evidence of variable proton biological effectiveness in pediatric patients treated for ependymoma

Radiother Oncol. 2016 Dec;121(3):395-401. doi: 10.1016/j.radonc.2016.11.001. Epub 2016 Nov 16.

Abstract

Background and purpose: A constant relative biological effectiveness (RBE) is used for clinical proton therapy; however, experimental evidence indicates that RBE can vary. We analyzed pediatric ependymoma patients who received proton therapy to determine if areas of normal tissue damage indicated by post-treatment image changes were associated with increased biological dose effectiveness.

Material and methods: Fourteen of 34 children showed T2-FLAIR hyperintensity on post-treatment magnetic resonance (MR) images. We delineated regions of treatment-related change and calculated dose and linear energy transfer (LET) distributions with Monte Carlo. Voxel-level image change data were fit to a generalized linear model incorporating dose and LET. Cross-validation was used to determine model parameters and for receiver operating characteristic curve analysis. Tolerance dose (TD50; dose at which 50% of patients would experience toxicity) was interpolated from the model.

Results: Image changes showed dependence on increasing LET and dose. TD50 decreased with increasing LET, indicating an increase in biological dose effectiveness. The cross-validated area under the curve for the model was 0.91 (95% confidence interval 0.88-0.94).

Conclusions: Our correlation of changes on MR images after proton therapy with increased LET constitutes the first clinical evidence of variable proton biological effectiveness.

Keywords: Biological effectiveness; Pediatric; Proton therapy.

MeSH terms

  • Child
  • Child, Preschool
  • Ependymoma / diagnostic imaging
  • Ependymoma / radiotherapy*
  • Female
  • Humans
  • Infant
  • Linear Energy Transfer
  • Linear Models
  • Magnetic Resonance Imaging
  • Male
  • Monte Carlo Method
  • Organs at Risk / radiation effects
  • Prospective Studies
  • Proton Therapy / adverse effects
  • Proton Therapy / methods*
  • Radiotherapy Dosage
  • Relative Biological Effectiveness