Patient's weight can decide about spending millions on enzyme replacement therapy in MPS II

Affiliations

• ¹ Department of Medical Genetics, Jagiellonian University, Medical College, Krakow, Poland.
• ² School of Medicine in Katowice, Department of Paediatrics and Developmental Age Neurology, Medical University of Silesia, Katowice, Poland.
• ³ Department of Pediatric Gastroenterology and Metabolism, Medical University, Poznan, Poland.
• ⁴ Department of Pediatrics, Nutrition and Metabolic Diseases, The Children's Memorial Health Institute, Warszawa, Poland.
• ⁵ Metabolic Department, Polish Mother's Health Memorial Institute, Lodz, Poland.
• ⁶ Screening Department, Institute of Mother and Child, Warszawa, Poland.
• ⁷ Department of Paediatric Endocrinology and Diabetology, Pomeranian Medical University in Szczecin, Poland.