Alpha-1-anti-trypsin-Fc fusion protein ameliorates gouty arthritis by reducing release and extracellular processing of IL-1β and by the induction of endogenous IL-1Ra

Ann Rheum Dis. 2016 Jun;75(6):1219-27. doi: 10.1136/annrheumdis-2014-206966. Epub 2015 Jul 14.

Abstract

Objectives: In the present study, we generated a new protein, recombinant human alpha-1-anti-trypsin (AAT)-IgG1 Fc fusion protein (AAT-Fc), and evaluated its properties to suppress inflammation and interleukin (IL)-1β in a mouse model of gouty arthritis.

Methods: A combination of monosodium urate (MSU) crystals and the fatty acid C16.0 (MSU/C16.0) was injected intra-articularly into the knee to induce gouty arthritis. Joint swelling, synovial cytokine production and histopathology were determined after 4 h. AAT-Fc was evaluated for inhibition of MSU/C16.0-induced IL-1β release from human blood monocytes and for inhibition of extracellular IL-1β precursor processing.

Results: AAT-Fc markedly suppressed MSU/C16.0-induced joint inflammation by 85-91% (p<0.001). Ex vivo production of IL-1β and IL-6 from cultured synovia were similarly reduced (63% and 65%, respectively). The efficacy of 2.0 mg/kg AAT-Fc in reducing inflammation was comparable to 80 mg/kg of plasma-derived AAT. Injection of AAT-Fc into mice increased circulating levels of endogenous IL-1 receptor antagonist by fourfold. We also observed that joint swelling was reduced by 80%, cellular infiltration by 95% and synovial production of IL-1β by 60% in transgenic mice expressing low levels of human AAT. In vitro, AAT-Fc reduced MSU/C16.0-induced release of IL-1β from human blood monocytes and inhibited proteinase-3-mediated extracellular processing of the IL-1β precursor into active IL-1β.

Conclusions: A single low dose of AAT-Fc is highly effective in reducing joint inflammation in this model of acute gouty arthritis. Considering the long-term safety of plasma-derived AAT use in humans, subcutaneous AAT-Fc emerges as a promising therapy for gout attacks.

Keywords: Cytokines; Gout; Inflammation; Treatment.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Arthritis, Experimental / drug therapy*
  • Arthritis, Experimental / immunology
  • Arthritis, Experimental / pathology
  • Arthritis, Gouty / drug therapy*
  • Arthritis, Gouty / immunology
  • Arthritis, Gouty / pathology
  • Cells, Cultured
  • Dose-Response Relationship, Drug
  • Drug Evaluation, Preclinical / methods
  • Gout Suppressants / administration & dosage
  • Gout Suppressants / pharmacology
  • Gout Suppressants / therapeutic use*
  • Humans
  • Immunoglobulin Fc Fragments / administration & dosage
  • Immunoglobulin Fc Fragments / pharmacology
  • Immunoglobulin Fc Fragments / therapeutic use*
  • Injections, Intra-Articular
  • Injections, Intraperitoneal
  • Interleukin 1 Receptor Antagonist Protein / biosynthesis*
  • Interleukin-1beta / antagonists & inhibitors*
  • Interleukin-1beta / metabolism
  • Lipopolysaccharide Receptors / analysis
  • Male
  • Mice, Inbred C57BL
  • Mice, Transgenic
  • Monocytes / drug effects
  • Monocytes / immunology
  • Recombinant Fusion Proteins / administration & dosage
  • Recombinant Fusion Proteins / pharmacology
  • Recombinant Fusion Proteins / therapeutic use*
  • alpha 1-Antitrypsin / administration & dosage
  • alpha 1-Antitrypsin / pharmacology
  • alpha 1-Antitrypsin / therapeutic use*

Substances

  • Gout Suppressants
  • Il1rn protein, mouse
  • Immunoglobulin Fc Fragments
  • Interleukin 1 Receptor Antagonist Protein
  • Interleukin-1beta
  • Lipopolysaccharide Receptors
  • Recombinant Fusion Proteins
  • alpha 1-Antitrypsin
  • alpha-1-anti-trypsin-IgG1 Fc fusion protein