Fibrosis progression according to epithelial-mesenchymal transition profile: a randomized trial of everolimus versus CsA

Am J Transplant. 2015 May;15(5):1303-12. doi: 10.1111/ajt.13132. Epub 2015 Mar 23.

Abstract

Markers of epithelial-mesenchymal transition (EMT) may identify patients at high risk of graft fibrogenesis who could benefit from early calcineurin inhibitor (CNI) withdrawal. In a randomized, open-label, 12-month trial, de novo kidney transplant patients received cyclosporine, enteric-coated mycophenolate sodium (EC-MPS) and steroids to month 3. Patients were stratified as EMT+ or EMT- based on month 3 biopsy, then randomized to start everolimus with half-dose EC-MPS (720 mg/day) and cyclosporine withdrawal (CNI-free) or continue cyclosporine with standard EC-MPS (CNI). The primary endpoint was progression of graft fibrosis (interstitial fibrosis/tubular atrophy [IF/TA] grade increase ≥1 between months 3-12) in EMT+ patients. 194 patients were randomized (96 CNI-free, 98 CNI); 153 (69 CNI-free, 84 CNI) were included in histological analyses. Fibrosis progression occurred in 46.2% (12/26) CNI-free EMT+ patients versus 51.6% (16/31) CNI EMT+ patients (p = 0.68). Biopsy-proven acute rejection (BPAR, including subclinical events) occurred in 25.0% and 5.1% of CNI-free and CNI patients, respectively (p < 0.001). In conclusion, early CNI withdrawal with everolimus initiation does not prevent interstitial fibrosis. Using this CNI-free protocol, in which everolimus exposure was relatively low and administered with half-dose EC-MPS, CNI-free patients were overwhelmingly under-immunosuppressed and experienced an increased risk of BPAR.

Keywords: calcineurin inhibitor:cyclosporine A (CsA); fibrosis; immunosuppressant.

Publication types

  • Randomized Controlled Trial
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Aged
  • Biopsy
  • Calcineurin Inhibitors / administration & dosage
  • Cyclosporine / administration & dosage*
  • Disease Progression
  • Epithelial-Mesenchymal Transition / drug effects*
  • Everolimus / administration & dosage*
  • Female
  • Fibrosis
  • Graft Survival
  • Humans
  • Immunosuppression Therapy
  • Inflammation / pathology
  • Kidney / pathology*
  • Kidney Transplantation*
  • Male
  • Middle Aged
  • Prospective Studies
  • Renal Insufficiency / surgery*
  • Risk Factors
  • Treatment Outcome

Substances

  • Calcineurin Inhibitors
  • Cyclosporine
  • Everolimus