Short communication: Efficiently inhibiting HIV-1 replication by a prototype foamy virus vector expressing novel H1 promoter-driven short hairpin RNAs

AIDS Res Hum Retroviruses. 2015 Feb;31(2):183-8. doi: 10.1089/AID.2014.0217. Epub 2015 Jan 22.

Abstract

RNA interference has shown great potential for the treatment of HIV-1. Vectors derived from prototype foamy viruses (PFVs) with a nonpathogenic nature are very promising gene transfer vehicles in anti-HIV gene therapy. In this article, three short hairpin RNAs (shRNAs) targeting the conserved regions of the HIV-1NL4-3 5' long terminal repeat (LTR) were first designed. We then constructed novel recombinant PFV vector plasmids, p▵Φ-H1-shRNAs, expressing these shRNAs under the control of the H1 RNA promoter. To detect the efficacy of these ▵Φ-H1-shRNAs for the inhibition of HIV-1 replication, we performed a dual-luciferase reporter assay, RT-qPCR, ELISA, western blotting, and a lactate dehydrogenase (LDH) assay by transient transfection in 293T cells. The results suggest that these novel shRNAs driven by PFV vectors inhibit HIV-1 replication efficiently without cytotoxicity, with shRNA3 being the most effective. In addition, we analyzed the shRNA target sites in the 5' LTR of HIV-1 strains other than HIV-1NL4-3 and found that these shRNAs may possibly inhibit other HIV-1 strains.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Anti-HIV Agents / metabolism*
  • Biological Products / metabolism
  • Blotting, Western
  • Cell Line
  • Cell Survival / drug effects
  • Drug Carriers*
  • Enzyme-Linked Immunosorbent Assay
  • Gene Expression
  • Gene Expression Profiling
  • Genetic Therapy / methods*
  • Genetic Vectors
  • HIV-1 / drug effects*
  • HIV-1 / genetics
  • Humans
  • L-Lactate Dehydrogenase / analysis
  • Promoter Regions, Genetic
  • RNA, Small Interfering / genetics
  • RNA, Small Interfering / metabolism*
  • Real-Time Polymerase Chain Reaction
  • Spumavirus / genetics
  • T-Lymphocytes / physiology*
  • T-Lymphocytes / virology*

Substances

  • Anti-HIV Agents
  • Biological Products
  • Drug Carriers
  • RNA, Small Interfering
  • L-Lactate Dehydrogenase