Fertility sparing treatment of complex atypical hyperplasia and low grade endometrial cancer using oral progestin

Gynecol Oncol. 2014 May;133(2):229-33. doi: 10.1016/j.ygyno.2014.02.020. Epub 2014 Feb 19.

Abstract

Objective: Oral progestin is an alternative to hysterectomy for women with complex atypical hyperplasia (CAH) or grade one endometrial cancer (G1EC) who wish fertility preservation. We evaluated treatment efficacy and fertility outcomes in this population.

Methods: Women <45 y treated with oral progestin for CAH or G1EC were identified from two cancer centers. Data were obtained from medical records and telephone questionnaires. Time until complete response (CR), and from CR until recurrence was censored for patients without events and analyzed for associations with patient and treatment characteristics; cumulative incidence functions were used to estimate event probability over time.

Results: 44 patients were identified, 19 (43%) with CAH and 25 (57%) with G1EC. Median age was 36.5 y (26-44). 24 (55%) achieved CR (median time: 5.7 months). Older age was associated with a lower likelihood of CR (HR 0.84, p=0.0003, 95% CI, 0.8-0.9). CR probability appeared to plateau after 12 months of therapy. Among those with CR, 13 (54%) recurred (median time 3.5 y). 24 patients (55%) underwent hysterectomy; 3 (13%) were upstaged. 11 (25%) underwent fertility treatment with the following outcomes: 6 (55%) no pregnancy, 2 (18%) at least one live infant, and 3 (27%) spontaneous abortion. One achieved a live birth without intervention.

Conclusion: Oral progestin is an effective temporizing fertility-sparing treatment for women with CAH/G1EC. Fertility specialist involvement is recommended due to the low live birth rate without intervention. Progestin therapy should be re-evaluated at 1 year in non-responders due to a low probability of success. Hysterectomy is recommended after childbearing due to a high recurrence rate.

Keywords: Conservative treatment; Endometrial atypical hyperplasia; Endometrial cancer; Fertility sparing; Progestin therapy.

Publication types

  • Observational Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Antineoplastic Agents, Hormonal / therapeutic use*
  • Carcinoma, Endometrioid / drug therapy*
  • Carcinoma, Endometrioid / pathology
  • Endometrial Hyperplasia / drug therapy*
  • Endometrial Neoplasms / drug therapy*
  • Endometrial Neoplasms / pathology
  • Female
  • Fertility Preservation / methods
  • Humans
  • Hysterectomy / statistics & numerical data
  • Medroxyprogesterone Acetate / therapeutic use*
  • Megestrol Acetate / therapeutic use*
  • Neoplasm Grading
  • Organ Sparing Treatments / methods
  • Pregnancy
  • Pregnancy Outcome
  • Pregnancy Rate
  • Reproductive Techniques, Assisted / statistics & numerical data
  • Retrospective Studies
  • Treatment Outcome

Substances

  • Antineoplastic Agents, Hormonal
  • Medroxyprogesterone Acetate
  • Megestrol Acetate