Small molecule screening in human induced pluripotent stem cell-derived terminal cell types

J Biol Chem. 2014 Feb 21;289(8):4562-70. doi: 10.1074/jbc.R113.529156. Epub 2013 Dec 20.

Abstract

A need for better clinical outcomes has heightened interest in the use of physiologically relevant human cells in the drug discovery process. Patient-specific human induced pluripotent stem cells may offer a relevant, robust, scalable, and cost-effective model of human disease physiology. Small molecule high throughput screening in human induced pluripotent stem cell-derived cells with the intent of identifying novel therapeutic compounds is starting to influence the drug discovery process; however, the use of these cells presents many high throughput screening development challenges. This technology has the potential to transform the way drug discovery is performed.

Keywords: Drug Action; Drug Development; Drug Discovery; Drug Screening; Stem Cells.

Publication types

  • Review

MeSH terms

  • High-Throughput Screening Assays / methods*
  • Humans
  • Induced Pluripotent Stem Cells / cytology*
  • Small Molecule Libraries / analysis*

Substances

  • Small Molecule Libraries