Inhibition of CatA: an emerging strategy for the treatment of heart failure

Future Med Chem. 2013 Mar;5(4):399-409. doi: 10.4155/fmc.13.24.

Abstract

The lysosomal serine carboxypeptidase CatA has a very important and well-known structural function as well as a, so far, less explored catalytic function. A complete loss of the CatA protein results in the lysosomal storage disease galactosialidosis caused by intralysosomal degradation of β-galactosidase and neuraminidase 1. However, mice with a catalytically inactive CatA enzyme show no signs of this disease. This observation establishes a clear distinction between structural and catalytic functions of the CatA enzyme. Recently, several classes of orally bioavailable synthetic inhibitors of CatA have been identified. Pharmacological studies in rodents indicate a remarkable influence of CatA inhibition on cardiovascular disease progression and identify CatA as a promising novel target for the treatment of heart failure.

MeSH terms

  • Animals
  • Biological Products / chemistry
  • Biological Products / pharmacology
  • Biological Products / therapeutic use
  • Cathepsin A / analysis
  • Cathepsin A / antagonists & inhibitors*
  • Cathepsin A / metabolism
  • Enzyme Inhibitors / chemistry*
  • Enzyme Inhibitors / pharmacology
  • Enzyme Inhibitors / therapeutic use*
  • Heart / drug effects
  • Heart Failure / drug therapy*
  • Heart Failure / enzymology*
  • Humans
  • Mice
  • Models, Molecular
  • Molecular Targeted Therapy / methods
  • Peptidomimetics / chemistry
  • Peptidomimetics / pharmacology
  • Peptidomimetics / therapeutic use
  • Rats
  • Small Molecule Libraries / chemistry
  • Small Molecule Libraries / pharmacology
  • Small Molecule Libraries / therapeutic use
  • Substrate Specificity

Substances

  • Biological Products
  • Enzyme Inhibitors
  • Peptidomimetics
  • Small Molecule Libraries
  • Cathepsin A