Marrow signal changes observed in follow-up whole-body MRI studies in children and young adults with neurofibromatosis type 1 treated with imatinib mesylate (Gleevec) for plexiform neurofibromas

Pediatr Radiol. 2012 Oct;42(10):1218-22. doi: 10.1007/s00247-012-2440-0. Epub 2012 Jun 22.

Abstract

Background: We observed bone marrow signal changes (BMSC) in patients with plexiform neurofibromas after treatment with imatinib mesylate (Gleevec).

Objective: To evaluate the pattern and natural history of BMSC.

Materials and methods: The data were obtained from a pilot study of imatinib mesylate in patients with plexiform neurofibromas. All patients underwent baseline and sequential whole-body STIR 1.5-T MRI after treatment. The bone marrow signal on MRI was evaluated for abnormalities, location and pattern, and any change on follow-up studies.

Results: The study group included 16 patients (8 males) with a median age of 14 years (range 4 to 25 years). The mean whole-body MRI follow-up duration was 1.9 years. Of the 16 patients, 14 (88%) developed BMSC. The signal change was asymmetrical in 9 of the 14 patients (64%). The appendicular skeleton was involved in all 14 patients and the axial skeleton in 3 patients (21%). BMSC was followed in 13 patients and decreased signal was seen in 9 patients (69%) after a mean duration of 1.3 years of treatment (range 0.6 to 2.9 years); no complications were observed.

Conclusion: BMSC appeared in most patients with neurofibromatosis type 1 following treatment with imatinib mesylate. BMSC was unusually asymmetrical and involved the lower extremities. On follow-up, BMSC often showed a decrease without complications.

Publication types

  • Clinical Trial

MeSH terms

  • Adolescent
  • Adult
  • Antineoplastic Agents / therapeutic use
  • Benzamides
  • Bone Marrow / drug effects
  • Bone Marrow / pathology*
  • Child
  • Child, Preschool
  • Female
  • Humans
  • Imatinib Mesylate
  • Magnetic Resonance Imaging / instrumentation
  • Male
  • Neurofibroma, Plexiform / drug therapy*
  • Neurofibroma, Plexiform / etiology
  • Neurofibroma, Plexiform / pathology*
  • Neurofibromatosis 1 / complications
  • Neurofibromatosis 1 / drug therapy*
  • Neurofibromatosis 1 / pathology*
  • Pilot Projects
  • Piperazines / therapeutic use*
  • Pyrimidines / therapeutic use*
  • Treatment Outcome
  • Whole Body Imaging / methods
  • Young Adult

Substances

  • Antineoplastic Agents
  • Benzamides
  • Piperazines
  • Pyrimidines
  • Imatinib Mesylate