X-linked hyper IgM syndrome: a novel sequence variant associated with an atypical mild phenotype

J Pediatr Hematol Oncol. 2012 Jul;34(5):e212-4. doi: 10.1097/MPH.0b013e318241fa1b.

Abstract

X-linked hyper IgM syndrome is associated with abnormalities in the gene encoding CD40 ligand (CD40LG). A typical phenotype evolves during infancy in affected males. This phenotype includes neutropenia, dysgammaglobulinemia, bacterial sinopulmonary infections, and opportunistic infections. In the absence of the typical phenotypic features, clinicians must maintain a high level of suspicion for X-linked hyper IgM syndrome. We describe a unique hemizygous CD40LG mutation which was discovered in a 12-year-old boy with chronic severe neutropenia, a normal IgG level, and absence of sinopulmonary or opportunistic infections. The clinical implications of this mutation and associated atypical phenotype are discussed.

Publication types

  • Case Reports

MeSH terms

  • CD40 Ligand / genetics*
  • Child
  • Humans
  • Hyper-IgM Immunodeficiency Syndrome, Type 1 / genetics*
  • Male
  • Mutation*
  • Neutropenia / etiology
  • Phenotype

Substances

  • CD40 Ligand