"Picolog," a synthetically-available bryostatin analog, inhibits growth of MYC-induced lymphoma in vivo

Oncotarget. 2012 Jan;3(1):58-66. doi: 10.18632/oncotarget.438.

Abstract

Bryostatin 1 is a naturally occurring complex macrolide with potent anti-neoplastic activity. However, its extremely low natural occurrence has impeded clinical advancement. We developed a strategy directed at the design of simplified and synthetically more accessible bryostatin analogs. Our lead analog, "picolog", can be step-economically produced. Picolog, compared to bryostatin, exhibited superior growth inhibition of MYC-induced lymphoma in vitro. A key mechanism of picolog's (and bryostatin's) activity is activation of PKC. A novel nano-immunoassay (NIA) revealed that picolog treatment increased phospho-MEK2 in the PKC pathway. Moreover, the inhibition of PKC abrogated picolog's activity. Finally, picolog was highly potent at 100 micrograms/kg and well tolerated at doses ranging from 100 micrograms/kg to 1 milligram/kg in vivo for the treatment of our aggressive model of MYC-induced lymphoma. We provide the first in vivo validation that the bryostatin analog, picolog, is a potential therapeutic agent for the treatment of cancer and other diseases.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antineoplastic Agents / chemical synthesis
  • Antineoplastic Agents / chemistry
  • Antineoplastic Agents / pharmacology
  • Bryostatins / chemical synthesis
  • Bryostatins / chemistry
  • Bryostatins / pharmacology*
  • Cell Growth Processes / drug effects*
  • Cell Transformation, Neoplastic / genetics
  • Cells, Cultured
  • Down-Regulation / drug effects
  • Female
  • Genes, myc / physiology*
  • Humans
  • Jurkat Cells
  • Lymphoma / genetics*
  • Lymphoma / pathology*
  • Mice
  • Models, Biological
  • Transfection
  • Xenograft Model Antitumor Assays

Substances

  • Antineoplastic Agents
  • Bryostatins
  • picolog