Congenital diaphragmatic hernia in Smith-Magenis syndrome: a possible locus at chromosome 17p11.2

Am J Med Genet A. 2011 Nov;155A(11):2816-20. doi: 10.1002/ajmg.a.34247. Epub 2011 Sep 30.

Abstract

We report on a 7-month-old girl with Smith-Magenis syndrome (SMS) due to a 4.76-Mb deletion of 17p12-17p11.2 detected by array comparative genomic hybridization. She was also affected with a left-sided congenital diaphragmatic hernia (CDH) and cardiac anomalies including an atypical atrioventricular canal defect and a cleft mitral valve. To our knowledge, this is the first reported case of a patient with both SMS and CDH. There are numerous chromosomal regions in which duplications, deletions, inversions, or translocations have been associated with CDH, but none have previously been reported at or close to 17p11.2. We discuss candidate genes for the diaphragmatic defect in this patient. Our case demonstrates that it is important to consider the possibility of SMS in non-isolated cases of diaphragmatic hernia.

Publication types

  • Case Reports
  • Research Support, N.I.H., Extramural

MeSH terms

  • Chromosome Deletion*
  • Chromosomes, Human, Pair 17 / genetics*
  • Comparative Genomic Hybridization
  • Female
  • Hernia, Diaphragmatic / genetics
  • Hernia, Diaphragmatic / pathology
  • Hernias, Diaphragmatic, Congenital*
  • Heterozygote
  • Humans
  • Infant
  • Infant, Newborn
  • Mitral Valve / abnormalities
  • Physical Examination
  • Polymorphism, Single Nucleotide
  • Smith-Magenis Syndrome / genetics*
  • Smith-Magenis Syndrome / pathology
  • Trans-Activators
  • Transcription Factors / genetics
  • Ubiquitin / genetics

Substances

  • RAI1 protein, human
  • Trans-Activators
  • Transcription Factors
  • UBB protein, human
  • Ubiquitin