Effect of stem cell source on outcomes after unrelated donor transplantation in severe aplastic anemia

Blood. 2011 Sep 1;118(9):2618-21. doi: 10.1182/blood-2011-05-354001. Epub 2011 Jun 15.

Abstract

Outcome after unrelated donor bone marrow (BM) transplantation for severe aplastic anemia (SAA) has improved, with survival rates now approximately 75%. Increasing use of peripheral blood stem and progenitor cells (PBPCs) instead of BM as a graft source prompted us to compare outcomes of PBPC and BM transplantation for SAA. We studied 296 patients receiving either BM (n = 225) or PBPC (n = 71) from unrelated donors matched at human leukocyte antigen-A, -B, -C, -DRB1. Hematopoietic recovery was similar after PBPC and BM transplantation. Grade 2 to 4 acute graft-versus-host disease risks were higher after transplantation of PBPC compared with BM (hazard ratio = 1.68, P = .02; 48% vs 31%). Chronic graft-versus-host disease risks were not significantly different after adjusting for age at transplantation (hazard ratio = 1.39, P = .14). Mortality risks, independent of age, were higher after PBPC compared with BM transplantation (hazard ratio = 1.62, P = .04; 76% vs 61%). These data indicate that BM is the preferred graft source for unrelated donor transplantation in SAA.

Publication types

  • Comparative Study
  • Evaluation Study
  • Research Support, N.I.H., Extramural
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Adolescent
  • Adult
  • Aged
  • Aged, 80 and over
  • Anemia, Aplastic / mortality
  • Anemia, Aplastic / surgery*
  • Bone Marrow Transplantation* / adverse effects
  • Bone Marrow Transplantation* / statistics & numerical data
  • Child
  • Child, Preschool
  • Female
  • Graft Survival
  • Graft vs Host Disease / epidemiology
  • Histocompatibility
  • Humans
  • Infant
  • Kaplan-Meier Estimate
  • Karnofsky Performance Status
  • Male
  • Middle Aged
  • Organ Specificity
  • Peripheral Blood Stem Cell Transplantation* / adverse effects
  • Peripheral Blood Stem Cell Transplantation* / statistics & numerical data
  • Proportional Hazards Models
  • Registries
  • Retrospective Studies
  • Tissue Donors*
  • Transplantation Conditioning / methods
  • Transplantation, Homologous / statistics & numerical data
  • Treatment Outcome
  • Young Adult