Discovery of a 3-pyridylacetic acid derivative (TAK-100) as a potent, selective and orally active dipeptidyl peptidase IV (DPP-4) inhibitor

J Med Chem. 2011 Feb 10;54(3):831-50. doi: 10.1021/jm101236h. Epub 2011 Jan 10.

Abstract

Inhibition of dipeptidyl peptidase IV (DPP-4) is an exciting new approach for the treatment of diabetes. To date there has been no DPP-4 chemotype possessing a carboxy group that has progressed into clinical trials. Originating from the discovery of the structurally novel quinoline derivative 1, we designed novel pyridine derivatives containing a carboxy group. In our design, the carboxy group interacted with the targeted amino acid residues around the catalytic region and thereby increased the inhibitory activity. After further optimization, we identified a hydrate of [5-(aminomethyl)-6-(2,2-dimethylpropyl)-2-ethyl-4-(4-methylphenyl)pyridin-3-yl]acetic acid (30c) as a potent and selective DPP-4 inhibitor. The desired interactions with the critical active-site residues, such as a salt-bridge interaction with Arg125, were confirmed by X-ray cocrystal structure analysis. In addition, compound 30c showed a desired preclinical safety profile, and it was encoded as TAK-100.

MeSH terms

  • Acetates / chemical synthesis*
  • Acetates / pharmacokinetics
  • Acetates / pharmacology
  • Animals
  • Catalytic Domain
  • Crystallography, X-Ray
  • Dipeptidyl-Peptidase IV Inhibitors / chemical synthesis*
  • Dipeptidyl-Peptidase IV Inhibitors / pharmacokinetics
  • Dipeptidyl-Peptidase IV Inhibitors / pharmacology
  • Dogs
  • Female
  • Glucose Tolerance Test
  • Humans
  • Hydrophobic and Hydrophilic Interactions
  • Hypoglycemic Agents / chemical synthesis*
  • Hypoglycemic Agents / pharmacokinetics
  • Hypoglycemic Agents / pharmacology
  • Models, Molecular
  • Protein Conformation
  • Pyridines / chemical synthesis*
  • Pyridines / pharmacokinetics
  • Pyridines / pharmacology
  • Quinolines / chemical synthesis
  • Quinolines / pharmacokinetics
  • Quinolines / pharmacology
  • Rats
  • Rats, Wistar
  • Structure-Activity Relationship

Substances

  • 5-(aminomethyl)-6-(2,2-dimethylpropyl)-2-ethyl-4-(4-methylphenyl)pyridin-3-ylacetic acid
  • Acetates
  • Dipeptidyl-Peptidase IV Inhibitors
  • Hypoglycemic Agents
  • Pyridines
  • Quinolines

Associated data

  • PDB/3O95
  • PDB/3O9V