Transduction of PACAP38 protects primary cortical neurons from neurotoxic injury

Neurosci Lett. 2008 Dec 19;448(1):52-5. doi: 10.1016/j.neulet.2008.10.021. Epub 2008 Oct 14.

Abstract

Neurotrophic factors such as pituitary adenylate cyclase activating polypeptide (PACAP38) are promising therapeutics for neurodegenerative diseases. However, delivery of trophic factors into brain neurons remains a challenge. The objective of this study is to determine whether adeno-associated virus (AAV) can mediate PACAP38 gene delivery into neurons in vitro and if transduction of AAV/PACAP38 into cortical neurons protects cells against neurotoxic insult. Primary cortical neuronal cultures are transduced with rAAV/PACAP38/GFP and cell survival against the nitric oxide releasing neurotoxin sodium nitroprusside (SNP) determined. GFP expression, a surrogate marker for successful transduction, is detected using fluorescent microscopy. The results show expression of GFP transgene and AAV capsid proteins in neurons. PACAP38 transduction significantly increases cell survival of neurons exposed to SNP. These results support the feasibility of using AAV-mediated delivery of PACAP38 to enhance neuronal survival and suggest that AAV-delivered PACAP38 maybe a therapeutic strategy for neurodegenerative diseases.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Analysis of Variance
  • Animals
  • Cell Survival / genetics
  • Cerebral Cortex / cytology*
  • Embryo, Mammalian
  • Fatty Acids, Monounsaturated
  • Green Fluorescent Proteins / genetics
  • Indoles
  • Neurons / drug effects
  • Neurons / physiology*
  • Nitric Oxide Donors / toxicity
  • Nitroprusside / toxicity
  • Pituitary Adenylate Cyclase-Activating Polypeptide / genetics*
  • Quaternary Ammonium Compounds
  • Rats
  • Transduction, Genetic / methods*
  • Transfection / methods

Substances

  • Fatty Acids, Monounsaturated
  • Indoles
  • Nitric Oxide Donors
  • Pituitary Adenylate Cyclase-Activating Polypeptide
  • Quaternary Ammonium Compounds
  • Green Fluorescent Proteins
  • Nitroprusside
  • DAPI
  • 1,2-dioleoyloxy-3-(trimethylammonium)propane