A new point mutation in the 3,5,3'-triiodothyronine-binding domain of the c-erbA beta thyroid hormone receptor is tightly linked to generalized thyroid hormone resistance

J Clin Endocrinol Metab. 1991 Jan;72(1):32-8. doi: 10.1210/jcem-72-1-32.

Abstract

Two different mutations in the c-erbA beta thyroid hormone receptor have recently been reported as genetic abnormalities responsible for the syndrome of generalized thyroid hormone resistance (GTHR). We have now found in a third kindred, D, in which GTHR is inherited as a dominant disease, a new point mutation in the T3-binding domain of c-erbA beta. A guanine to cytosine base substitution at nucleotide position 1305, which altered codon-335 from glutamine (CAG) to histidine (CAC), was found in one allele of 10 affected members and was not found in 6 unaffected members. This C-1305 sequence was not present in 106 random alleles, indicating that it was a mutation in c-erbA beta, and it was tightly linked to GTHR in kindred D, with a maximum logarithm of the odds score of 4.19 at a recombination fraction of 0. The tight linkage result confirms that GTHR maps to the c-erbA beta locus in multiple kindreds. In view of the tight linkage between the C-1305 mutation and GTHR, and that this mutation is a nonconservative alteration in a crucial region of the T3-binding domain, it is probably the genetic defect in kindred D responsible for GTHR. The kindred D receptor appears to result in a different phenotype of tissue resistance compared to the previously reported kindred. A receptor with a mutation in the carboxy-terminus of c-erbA beta.

MeSH terms

  • Base Sequence
  • Binding Sites
  • Cytosine
  • Deoxyribonucleases, Type II Site-Specific
  • Drug Resistance / genetics
  • Endocrine System Diseases / genetics*
  • Female
  • Humans
  • Lod Score
  • Male
  • Molecular Sequence Data
  • Mutation*
  • Pedigree
  • Pituitary Gland / drug effects
  • Proto-Oncogene Proteins / genetics*
  • Receptors, Thyroid Hormone / genetics*
  • Syndrome
  • Thyroid Hormones / blood
  • Thyroid Hormones / pharmacology*
  • Thyrotropin-Releasing Hormone
  • Triiodothyronine / metabolism*

Substances

  • Proto-Oncogene Proteins
  • Receptors, Thyroid Hormone
  • Thyroid Hormones
  • Triiodothyronine
  • Thyrotropin-Releasing Hormone
  • Cytosine
  • CAGCTG-specific type II deoxyribonucleases
  • Deoxyribonucleases, Type II Site-Specific