Tyrosine hydroxylase deficiency presenting with a biphasic clinical course

Neuropediatrics. 2007 Aug;38(4):213-5. doi: 10.1055/s-2007-991151.

Abstract

Tyrosine hydroxylase deficiency, a cause of the autosomal recessive form of L-DOPA responsive dystonia, has been associated with a broad spectrum of movement disorders and clinical courses. We describe a new patient presenting with an early onset spastic paraplegia who later developed a progressive generalized dystonic-dyskinetic syndrome. He markedly improved with a very low dosage of L-DOPA/carbidopa, while higher dosages were not tolerated. Two novel mutations (p.G414R/p.L510Q) were detected in the TH gene.

Publication types

  • Case Reports

MeSH terms

  • Adolescent
  • DNA Mutational Analysis / methods
  • Dopamine Agents / therapeutic use
  • Humans
  • Levodopa / therapeutic use
  • Male
  • Mutation
  • Paraplegia / drug therapy
  • Paraplegia / genetics*
  • Paraplegia / metabolism*
  • Tyrosine 3-Monooxygenase / deficiency*
  • Tyrosine 3-Monooxygenase / genetics

Substances

  • Dopamine Agents
  • Levodopa
  • Tyrosine 3-Monooxygenase