An RNA targeted to the HIV-1 LTR promoter modulates indiscriminate off-target gene activation

Nucleic Acids Res. 2007;35(21):7303-12. doi: 10.1093/nar/gkm847. Epub 2007 Oct 24.

Abstract

Transcriptional gene silencing (TGS) can be achieved by small RNAs targeted to upstream promoter regions. Previously we characterized siRNAs targeted to the HIV-1 long terminal repeat (LTR) promoter at site 247, and found that a 21-base antisense strand of siRNA-247 (LTR-247as) suppressed LTR-mediated expression. To characterize the specificity of LTR-247as, vectors expressing antisense RNAs targeted to a region spanning 50 bases up- and downstream of the 247 target site were generated. LTR-247as+7, a approximately 22 base antisense RNA that is shifted by only seven bases upstream of LTR-247as, showed a significant increase in LTR-driven reporter gene expression that was independent of cell type and active chromatin methyl-marks. Promoter-targeting siRNAs have been recently shown to induce gene activation. However, here we demonstrate gene activation via a sequence-specific off-target effect. Microarray analysis of LTR-247as+7-treated cultures resulted in the deregulation of approximately 185 genes. A gene of unknown function, C10orf76, was responsive to inhibition by LTR-247as+7 and the loss of C10orf76 resulted in the upregulation of several genes that were activated by LTR-247as+7. These data suggest caution when using short antisense RNAs or siRNAs designed to target promoter sequences, since promoter-targeted RNAs may have unintended inhibitory effects against factors with suppressive gene activity.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Gene Expression Profiling
  • Gene Expression Regulation, Viral
  • Genes, Reporter
  • HIV Long Terminal Repeat*
  • HIV-1 / genetics*
  • Histones / metabolism
  • Humans
  • Jurkat Cells
  • Luciferases / analysis
  • Luciferases / genetics
  • Promoter Regions, Genetic*
  • RNA Interference*
  • RNA, Small Interfering / chemistry
  • RNA, Small Interfering / metabolism*
  • RNA, Small Nuclear / antagonists & inhibitors
  • Transcriptional Activation*

Substances

  • Histones
  • RNA, Small Interfering
  • RNA, Small Nuclear
  • U6 small nuclear RNA
  • Luciferases