A case of incontinentia pigmenti in Japan and its genetic examination

Jpn J Ophthalmol. 2007 Mar-Apr;51(2):142-5. doi: 10.1007/s10384-006-0412-3. Epub 2007 Apr 6.

Abstract

Purpose: Incontinentia pigmenti (IP) is a rare X-linked dominant genodermatosis with approximately one-third of cases with associated ocular complications. Deletion of exons 4 to 10 of the nuclear factor kappaB essential modulator (NEMO) gene accounts for the majority of new mutations. The disease is more commonly found among Caucasians. We studied a case of an IP patient in Japan, and the genomic rearrangements.

Methods: An 11-month-old female infant exhibited the skin lesions of IP. Ocular findings were total retinal detachment with a retrolental fibrovascular mass in the right eye, and patchy retinal avascular zones and neovascularization in the left eye. The genomic rearrangement of NEMO was investigated by a polymerase chain reaction (PCR)-based diagnostic test. A skewed X-inactivation assay was also performed using the human androgen receptor gene as a genetic marker.

Results: Deletion of exons 4 to 10 in NEMO was detected in the proband and in other female members of her family. A complete skewing of the X-inactivation pattern causing IP was observed, indicating cells having no protection against apoptosis in response to tumor necrosis factor as the pathogenicity of the disease.

Conclusion: This is the first case report of a Japanese female phenotype demonstrating the common genomic rearrangement in the NEMO gene.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Chromosomes, Human, X / genetics*
  • Exons / genetics
  • Female
  • Gene Deletion*
  • Humans
  • I-kappa B Kinase / genetics*
  • Incontinentia Pigmenti / genetics*
  • Infant
  • Japan
  • Pedigree
  • Phenotype
  • Polymerase Chain Reaction
  • Receptors, Androgen / genetics
  • Retinal Diseases / genetics*
  • X Chromosome Inactivation / genetics*

Substances

  • AR protein, human
  • IKBKG protein, human
  • Receptors, Androgen
  • I-kappa B Kinase