Enzyme replacement for infantile Pompe disease: the first step toward a cure

Neurology. 2007 Jan 9;68(2):88-9. doi: 10.1212/01.wnl.0000253226.13795.40.
No abstract available

Publication types

  • Comment
  • Editorial
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Child
  • Glycogen Storage Disease Type II / drug therapy*
  • Humans
  • Palliative Care / methods*
  • Quality of Life*
  • Terminal Care / methods*
  • Treatment Outcome
  • alpha-Glucosidases / therapeutic use*

Substances

  • GAA protein, human
  • alpha-Glucosidases