Steroidogenic factor-1 (SF-1) and its relevance to pediatric endocrinology

Pediatr Endocrinol Rev. 2006 Jun;3(4):359-64.

Abstract

Steroidogenic factor-1 (SF-1) (NR5A1) is a member of the nuclear receptor superfamily that is expressed widely throughout the adrenal and reproductive axes during development and plays a central role in the function of these endocrine systems in post-natal and adult life. Much has been learned about the role of this transcription factor since its initial cloning in 1992, largely due to the creation of an Sf-1 (FtzF1) knockout mouse model, in vitro studies of nuclear receptor function and, more recently, following identification and characterization of patients with naturally-occurring SF-1 mutations. In this review, we will summarize how our knowledge of SF-1 in endocrine development and disease evolved to its current state, focusing on the spectrum of phenotypes associated with mutations in this transcription factor in patients who might present to a pediatric endocrinologist.

Publication types

  • Review

MeSH terms

  • Animals
  • Child
  • Endocrine System Diseases / genetics
  • Endocrine System Diseases / physiopathology*
  • Endocrinology*
  • Gonadal Dysgenesis / genetics
  • Gonadal Dysgenesis / physiopathology
  • Homeodomain Proteins / genetics
  • Homeodomain Proteins / physiology*
  • Humans
  • Pediatrics*
  • Receptors, Cytoplasmic and Nuclear / genetics
  • Receptors, Cytoplasmic and Nuclear / physiology*
  • Steroidogenic Factor 1
  • Transcription Factors / genetics
  • Transcription Factors / physiology*

Substances

  • Homeodomain Proteins
  • NR5A1 protein, human
  • Receptors, Cytoplasmic and Nuclear
  • Steroidogenic Factor 1
  • Transcription Factors
  • steroidogenic factor 1, mouse