Suppression of HIV-1 infection in primary CD4 T cells transduced with a self-inactivating lentiviral vector encoding a membrane expressed gp41-derived fusion inhibitor

Clin Immunol. 2005 Apr;115(1):26-32. doi: 10.1016/j.clim.2005.02.019.

Abstract

Peptidomimetics of HIV-1 gp41 sequences required for membrane fusion are potent inhibitors of HIV-1 entry. We hypothesize that expression of a membrane-bound gp41-derived fusion inhibitor will confer HIV-1 resistance to primary CD4 T cells. Efficient gene delivery and stable expression of a membrane-bound gp41-derived fusion inhibitor to primary CD4 T cells was accomplished using a self-inactivating lentiviral vector. A potent antiviral effect was observed when transduced CD4 T cells were challenged with a highly virulent CXCR4-tropic strain of HIV-1. Production of soluble p24 in the supernatant was inhibited 100-fold, and cytopathic effects were evident early in non-transduced cells and absent in transduced cells. Expression of the gp41 sequences was not detrimental to CD4 cells as transduced CD4 T cells exhibited a population doubling time that was equivalent to T cells transduced with a control vector. Results from this study support the rationale to use this lentiviral vector targeted at HIV entry as a potential gene therapy for HIV infection.

MeSH terms

  • Anti-HIV Agents / administration & dosage
  • CD4-Positive T-Lymphocytes / immunology*
  • CD4-Positive T-Lymphocytes / virology
  • Flow Cytometry
  • Genetic Therapy / methods*
  • Genetic Vectors / genetics
  • Genetic Vectors / immunology
  • HIV Core Protein p24 / immunology
  • HIV Envelope Protein gp41 / genetics*
  • HIV Envelope Protein gp41 / immunology
  • HIV Fusion Inhibitors / administration & dosage
  • HIV Infections / immunology
  • HIV Infections / therapy*
  • HIV-1 / immunology*
  • Humans
  • Kinetics
  • Lentivirus / genetics*
  • Lentivirus / immunology
  • Receptors, CXCR4 / immunology
  • Transduction, Genetic

Substances

  • Anti-HIV Agents
  • HIV Core Protein p24
  • HIV Envelope Protein gp41
  • HIV Fusion Inhibitors
  • Receptors, CXCR4