C29G in the iron-responsive element of L-ferritin: a new mutation associated with hyperferritinemia-cataract

Blood Cells Mol Dis. 2004 Jul-Aug;33(1):31-4. doi: 10.1016/j.bcmd.2004.04.010.

Abstract

Hyperferritinemia-cataract syndrome (HHCS) is a dominant disorder characterized by high serum ferritin and early onset of bilateral cataract. The disorder is caused by mutations in the iron-responsive element (IRE) of l-ferritin, which disrupt the postranscriptional control of l-ferritin synthesis. Here, we report a new (C>G) mutation which affects base 29 in the loop (c.-169C>G), previously unrecognized as essential for the stem loop stability. The mutation was identified in two members of an Italian family. Computer modeling and electrophoretic mobility shift assay (EMSA) confirm a decreased affinity of the C29G IRE for IRPs control proteins.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Apoferritins
  • Cataract / etiology*
  • Cataract / genetics
  • Electrophoretic Mobility Shift Assay
  • Family Health
  • Female
  • Ferritins / biosynthesis*
  • Ferritins / blood
  • Ferritins / genetics
  • Humans
  • Infant
  • Iron-Regulatory Proteins / metabolism
  • Italy
  • Male
  • Models, Molecular
  • Nucleic Acid Conformation
  • Point Mutation*
  • Protein Binding
  • Response Elements / genetics*

Substances

  • Iron-Regulatory Proteins
  • Ferritins
  • Apoferritins