Identification of synthetic endothelial cell-specific promoters by use of a high-throughput screen

J Virol. 2004 Jun;78(12):6209-21. doi: 10.1128/JVI.78.12.6209-6221.2004.

Abstract

Transcriptional targeting is a desirable property for many gene transfer applications. Because endothelial cells line most blood vessels, they are attractive candidates for the introduction of therapeutic gene products. As a proof-of-concept study, we attempted to identify a synthetic, endothelial cell-specific promoter by use of a high-throughput screen involving self-inactivating (SIN) human immunodeficiency virus type 1 (HIV-1)-based vectors. Select duplex oligodeoxynucleotides recognized by transcription factors and located 5' of endothelial cell-specific mRNA transcripts were randomly ligated and cloned upstream of a minimal ICAM-2 promoter driving enhanced green fluorescent protein (eGFP) in a SIN HIV-1-based vector. Vesicular stomatitis virus G protein-pseudotyped particles were prepared from a library of >10(6) vector recombinants and used to transduce an endothelial cell line. The highest eGFP expressers were repeatedly sorted, and the synthetic promoters were recovered and retested by a luciferase reporter. Several promoters were active and specific to endothelial cells of varied species, with high selectivity indexes and inducibility under hypoxia-mimetic conditions. One in particular was then introduced back into a SIN HIV-1-based vector to confirm its endothelial cell activity and specificity. This study suggests that SIN vectors may be used in a high-throughput manner to identify tissue-specific promoters of high activity, with potential applications for both transcriptional targeting and gene transfer.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Antigens, CD / chemistry
  • Antigens, CD / genetics
  • Base Sequence
  • Cell Adhesion Molecules / chemistry
  • Cell Adhesion Molecules / genetics
  • Endothelial Cells / virology*
  • Endothelium, Vascular / cytology
  • Endothelium, Vascular / virology
  • Gene Transfer Techniques
  • Genes, Synthetic*
  • Genetic Vectors*
  • Green Fluorescent Proteins
  • HIV Long Terminal Repeat
  • HIV-1 / genetics*
  • Humans
  • Luminescent Proteins / genetics
  • Molecular Sequence Data
  • Oligonucleotides
  • Promoter Regions, Genetic*

Substances

  • Antigens, CD
  • Cell Adhesion Molecules
  • ICAM2 protein, human
  • Luminescent Proteins
  • Oligonucleotides
  • Green Fluorescent Proteins