Inhibition of gene expression in Escherichia coli by antisense phosphorodiamidate morpholino oligomers

Antimicrob Agents Chemother. 2003 Oct;47(10):3233-9. doi: 10.1128/AAC.47.10.3233-3239.2003.

Abstract

Antisense phosphorodiamidate morpholino oligomers (PMOs) were tested for the ability to inhibit gene expression in Escherichia coli. PMOs targeted to either a myc-luciferase reporter gene product or 16S rRNA did not inhibit luciferase expression or growth. However, in a strain with defective lipopolysaccharide (lpxA mutant), which has a leaky outer membrane, PMOs targeted to the myc-luciferase or acyl carrier protein (acpP) mRNA significantly inhibited their targets in a dose-dependent response. A significant improvement was made by covalently joining the peptide (KFF)(3)KC to the end of PMOs. In strains with an intact outer membrane, (KFF)(3)KC-myc PMO inhibited luciferase expression by 63%. A second (KFF)(3)KC-PMO conjugate targeted to lacI mRNA induced beta-galactosidase in a dose-dependent response. The end of the PMO to which (KFF)(3)KC is attached affected the efficiency of target inhibition but in various ways depending on the PMO. Another peptide-lacI PMO conjugate was synthesized with the cationic peptide CRRRQRRKKR and was found not to induce beta-galactosidase. We conclude that the outer membrane of E. coli inhibits entry of PMOs and that (KFF)(3)KC-PMO conjugates are transported across both membranes and specifically inhibit expression of their genetic targets.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Acyl Carrier Protein / genetics
  • Acyl Carrier Protein / metabolism
  • Amino Acid Sequence
  • Bacterial Proteins / genetics
  • Base Sequence
  • Cell Membrane Permeability
  • Dose-Response Relationship, Drug
  • Escherichia coli / drug effects
  • Escherichia coli / genetics*
  • Escherichia coli / metabolism
  • Escherichia coli Proteins / chemistry
  • Gene Expression / drug effects
  • Genes, Reporter / drug effects
  • Genes, Reporter / genetics
  • Genes, myc / drug effects
  • Genes, myc / genetics
  • Lac Repressors
  • Luciferases / antagonists & inhibitors
  • Luciferases / genetics
  • Membrane Transport Proteins / genetics
  • Membrane Transport Proteins / metabolism
  • Morpholines / chemistry
  • Morpholines / metabolism
  • Morpholines / pharmacology*
  • Morpholinos
  • Oligonucleotides, Antisense / chemistry
  • Oligonucleotides, Antisense / metabolism
  • Oligonucleotides, Antisense / pharmacology*
  • RNA, Ribosomal, 16S / drug effects
  • RNA, Ribosomal, 16S / genetics
  • Repressor Proteins / genetics
  • beta-Galactosidase / metabolism

Substances

  • Acyl Carrier Protein
  • Bacterial Proteins
  • Escherichia coli Proteins
  • Lac Repressors
  • LacI protein, E coli
  • Membrane Transport Proteins
  • Morpholines
  • Morpholinos
  • Oligonucleotides, Antisense
  • RNA, Ribosomal, 16S
  • Repressor Proteins
  • Luciferases
  • beta-Galactosidase