Paramyotonia congenita due to a de novo mutation: a case report

Muscle Nerve. 2003 Aug;28(2):232-5. doi: 10.1002/mus.10396.

Abstract

A Japanese man with a negative family history of paramyotonia congenita (PMC) was evaluated for symptoms of cold-induced weakness and stiffness. Exercise testing revealed findings characteristic of PMC, and a genetic analysis was therefore performed. A well-known sodium channel mutation for PMC (T1313M) was identified in the patient, but was absent in his biological parents. These data demonstrate the occurrence of a de novo mutation, suggesting that evaluation for PMC should be performed in patients with typical symptoms even if the family history is negative.

Publication types

  • Case Reports

MeSH terms

  • Adult
  • Base Sequence
  • Electromyography
  • Exercise Test
  • Genetic Markers
  • Haplotypes
  • Humans
  • Male
  • Molecular Sequence Data
  • Muscle Weakness / etiology
  • Muscle Weakness / physiopathology
  • Mutation / genetics*
  • Mutation / physiology*
  • Myotonic Disorders / genetics*
  • NAV1.4 Voltage-Gated Sodium Channel
  • Pedigree
  • Reverse Transcriptase Polymerase Chain Reaction
  • Sodium Channels / genetics

Substances

  • Genetic Markers
  • NAV1.4 Voltage-Gated Sodium Channel
  • SCN4A protein, human
  • Sodium Channels