Spondyloenchondromatosis with D-2-hydroxyglutaric aciduria: a report of a second patient with this unusual combination

Clin Dysmorphol. 2003 Apr;12(2):95-9. doi: 10.1097/00019605-200304000-00004.

Abstract

Spondyloenchondromatosis (SEM) is a rare skeletal dysplasia which presents with multiple enchondromata in the metaphyses of the long bones associated with dysplastic vertebral bodies. It is probably heterogeneous. We have investigated and documented a male infant in South Africa with spondyloenchondromatosis and persistent D-2-hydroxyglutaric aciduria (D2HA). D2HA is a neurometabolic disorder whose enzymatic basis is still undefined. A girl in England with a similar clinical, radiological and biochemical phenotype has previously been reported by Talkhani et al. [(2000). Skel Radiol 7:215-2921]. There is at present a lack of a plausible pathogenetic relationship between the two components of the disorder but a contiguous gene syndrome or a pleiotropic gene could be considered. Whatever the underlying mechanism this case report confirms its nosological entity.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Arm / abnormalities*
  • Arm / diagnostic imaging
  • Brain / abnormalities
  • Brain / diagnostic imaging
  • Enchondromatosis / physiopathology*
  • Glutarates / metabolism*
  • Glutarates / urine
  • Humans
  • Infant
  • Leg / abnormalities*
  • Leg / diagnostic imaging
  • Lumbar Vertebrae / abnormalities
  • Lumbar Vertebrae / diagnostic imaging
  • Magnetic Resonance Imaging
  • Male
  • Radiography
  • Scapula / abnormalities
  • Scapula / diagnostic imaging

Substances

  • Glutarates
  • glutaric acid