Induction of T-cell tolerance to an MHC class I alloantigen by gene therapy

Blood. 2002 Jun 15;99(12):4394-9. doi: 10.1182/blood.v99.12.4394.

Abstract

Induction of immunologic tolerance to alloantigens is a major goal in the field of transplantation. Here, we demonstrate that efficient transduction and expression of a retrovirally transduced major histocompatibility complex (MHC) class I gene (H-2K(b)) in bone marrow (BM)-derived cells, resulting in a permanent state of hematopoietic molecular chimerism, induces stable tolerance to the transduced gene product. Reconstitution of lethally irradiated syngeneic recipients with BM transduced with virus encoding H-2K(b) resulted in life-long expression of the retroviral gene product on the surface of BM-derived hematopoietic lineages including Sca-1(+), lineage negative, hematopoietic progenitors. T cells from mice receiving MHC-transduced BM were unable to kill targets expressing H-2K(b) but were able to respond to third-party controls. Mice reconstituted with H-2K(b)-transduced BM exhibited long-term acceptance of H-2K(b) mismatched skin grafts but were able to rapidly reject third-party control grafts. Thus, gene therapy approaches may be used to induce T-cell tolerance.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, P.H.S.

MeSH terms

  • Animals
  • Bone Marrow Cells / metabolism
  • Bone Marrow Transplantation
  • Female
  • Genes, MHC Class I
  • Genetic Therapy* / methods
  • H-2 Antigens / genetics
  • H-2 Antigens / immunology
  • H-2 Antigens / therapeutic use
  • Histocompatibility Antigens Class I / genetics
  • Histocompatibility Antigens Class I / immunology*
  • Histocompatibility Antigens Class I / therapeutic use
  • Immune Tolerance*
  • Isoantigens / genetics
  • Isoantigens / immunology
  • Isoantigens / therapeutic use
  • Mice
  • Mice, Inbred Strains
  • Skin Transplantation / immunology
  • T-Lymphocytes / immunology*
  • Transduction, Genetic
  • Transplantation Chimera

Substances

  • H-2 Antigens
  • H-2Kb protein, mouse
  • Histocompatibility Antigens Class I
  • Isoantigens