Gene therapy of hematopoietic stem cells: strategies for improvement

News Physiol Sci. 2002 Jun:17:87-92. doi: 10.1152/nips.01343.2001.

Abstract

Gene therapy of hematopoietic stem cells (HSC) is limited by low frequency of the target cells, their quiescent nature, poor engraftment of treated HSC, and lack of a selective growth advantage of genetically modified cells. Lentiviral vectors combined with positive selection strategies using conditional cell-growth switches should allow for improvement.

Publication types

  • Review

MeSH terms

  • Genetic Therapy / methods*
  • Genetic Therapy / trends
  • Genetic Vectors
  • Hematopoietic Stem Cells / physiology*
  • Humans
  • Retroviridae / genetics