Clinical, biochemical and neuroradiological findings in L-2-hydroxyglutaric aciduria

Neurol Sci. 2000 Apr;21(2):103-8. doi: 10.1007/s100720070104.

Abstract

L-2-Hydroxyglutaric aciduria is a rare inborn error of metabolism, marked by a large and persistent increase of L-2-hydroxyglutaric acid in urine, blood and cerebrospinal fluid (CSF). We present clinical, biochemical and neuroradiological findings of seven Italian patients aged 4-19 years presenting at different stages of the disease. The disorder was characterized by a progressive neurological syndrome with cerebellar and pyramidal signs, mental deterioration, epilepsy and subcortical leukoencephalopathy on magnetic resonance imaging (MRI). We observed a good correlation between the severity of the disease and the extent of lesions on MRI. We report the result of the first positive prenatal diagnosis.

MeSH terms

  • Adolescent
  • Adult
  • Brain / pathology*
  • Child, Preschool
  • Female
  • Glutarates / cerebrospinal fluid
  • Glutarates / urine*
  • Humans
  • Magnetic Resonance Imaging*
  • Male
  • Nervous System Diseases / complications
  • Nervous System Diseases / diagnosis*
  • Nervous System Diseases / genetics
  • Nervous System Diseases / physiopathology
  • Neural Conduction
  • Prenatal Diagnosis
  • Syndrome

Substances

  • Glutarates
  • alpha-hydroxyglutarate